Velaglucerase alfa for injection / Gaucher Disease. Gaucher belongs to a group of conditions called Iysosomal storage disorders (LSDs). There are 3 main types of Gaucher disease:
Type 1 (Non-neuronopathic) – the most common type with variable symptoms and progression
Type 2 (Acute neuronopathic) – an acute, severe form affecting the central nervous system in babies and infants
Type 3 (Chronic neuronopathic) – a chronic form affecting the central nervous system, that progresses over time
Active principle: Velaglucerase alfa